QURE is sharpening its gene therapy focus through faster regulatory pathways, a streamlined business model and CNS pipeline expansion, with AMT-130 at the center.
QURE's AMT-130 is driving investor focus as FDA feedback, a targeted third-quarter 2026 filing and cash into 2029 shape its regulatory outlook.
uniQure N.V. (QURE) reached a significant support level, and could be a good pick for investors from a technical perspective.
| Biotechnology Industry | Healthcare Sector | Matthew Kapusta CEO | XFRA Exchange | NL0010696654 ISIN |
| NL Country | 221 Employees | - Last Dividend | 31 Jan 2014 Last Split | 20 Jun 2007 IPO Date |
uniQure N.V. is a pioneering company in the biotechnology sector, focused on the advancement of gene therapies for patients grappling with rare and severe illnesses. Since its inception in 1998, uniQure N.V. has been at the forefront of developing innovative treatments aimed at significantly improving the quality of life for patients around the globe. With its headquarters nestled in Amsterdam, the Netherlands, the company leverages cutting-edge science to tackle some of the most challenging medical conditions.
HEMGENIX: A groundbreaking treatment for hemophilia B, HEMGENIX has successfully completed its Phase III HOPE-B pivotal trial. This gene therapy offers a new lease of life for patients suffering from this rare bleeding disorder, potentially reducing the dependence on traditional hemophilia treatments.
AMT-130: A novel gene therapy approach for Huntington's disease, AMT-130 is currently under Phase I/II clinical study. This treatment represents hope for patients with Huntington's disease, aiming to significantly slow down or halt the progression of this devastating neurodegenerative disorder.
AMT-162: Targeting superoxide dismutase 1-amyotrophic lateral sclerosis (SOD1-ALS), AMT-162 is in preclinical trials. ALS, also known as Lou Gehrig's disease, is a condition that affects nerve cells in the brain and spinal cord, leading to loss of muscle control. AMT-162 is being developed to treat this specific form of ALS.
AMT-260: This candidate is in preclinical trials to address temporal lobe epilepsy, a condition that can cause severe and recurrent seizures. AMT-260 aims to provide a new therapeutic approach that could better manage or potentially cure this form of epilepsy.
AMT-191: In the preclinical trial stage, AMT-191 is geared towards the treatment of Fabry disease, a genetic disorder that impairs the body's ability to break down specific fatty substances. AMT-191 could offer a significant advancement in treating this disease.
AMT-161: Also in preclinical trials, AMT-161 is a therapy aimed at treating amyotrophic lateral sclerosis (ALS) caused by mutations. This gene therapy could provide a targeted approach to combat this devastating version of ALS.
AMT-240: Currently in preclinical trials, AMT-240 is being developed for autosomal dominant Alzheimer's disease. This innovative treatment could potentially slow or halt the progression of Alzheimer's in patients with a family history of the disease.
AMT-210: Dedicated to tackling Parkinson's disease, AMT-210 is in the preclinical trial phase. This therapy aims to offer a new disease-modifying treatment option for patients with Parkinson's, a neurodegenerative disorder characterized by the decline of motor function.